We report interim (provisional) data from a first-in-human phase I/II open-label, dose-optimization study investigating the safety and efficacy of mRNA-3927 for PA ...
Metabolic disorders and organic acidemias comprise a diverse group of inherited conditions in which enzymatic deficiencies disrupt normal metabolic pathways. Such deficiencies lead to the accumulation ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results