—Surveys of caregivers and health care providers reveal gaps in screening and management of neuropsychiatric and neurodevelopmental symptoms among patients with Duchenne muscular dystrophy in the ...
VIJAYAWADA: Founded by Sobharani Sunkara in 2019, the Amaravathi Rare Diseases Organisation (ARDO) has emerged as a beacon of hope for individuals suffering from muscular dystrophy (MD) in the State.
A new study describes a base editing method for treating spinal muscular atrophy (SMA). This supports early signs that “single-shot” treatments from clinical trials using genome editing technologies ...
The Emirates Drug Establishment (EDE) has announced the approval of Itvisma (onasemnogene abeparvovec), a gene therapy that uses an adeno-associated viral vector to treat spinal muscular atrophy (SMA) ...
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