Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...

British singer Jesy Nelson recently took to Instagram to share a devastating update about her 8-month-old twin daughters.

Jesy Nelson revealed her twin daughters have been diagnosed with spinal muscular atrophy (SMA) in an emotional video while ...

Please provide your email address to receive an email when new articles are posted on . The study included 58 individuals with SMA types 2 and 3 who were treated with IV apitegromab for 52 weeks. At ...

We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Patients treated with onasemnogene abeparvovec recorded ...